1. Home
  2. Health
  3. Rare Diseases

Sitosterolemia
Inherited metabolic defect

From , former About.com Guide

Updated: May 28, 2004

About.com Health's Disease and Condition content is reviewed by our Medical Review Board

Sitosterolemia is an inherited metabolic defect in which chemicals from plants, called sterols, are not broken down correctly by the body. This causes the sterols to accumulate in the blood, which can cause damage to body tissues.

It is not known how often sitosterolemia occurs. As of 2000, only about 40 people with sitosterolemia had been identified worldwide. It is thought that sitosterolemia is more often misdiagnosed as high blood cholesterol, one of the disease's effects in the body. The disease can become evident at any age.

Symptoms
There are several important symptoms of sitosterolemia:

  • High level of plant sterols in the blood; blood cholesterol may be normal to high
  • Lumps or bumps on the skin, called xanthomas. These often occur in the tendons of the hands and the Achilles tendons in the heel.
  • Arthritis, particularly in the knees and ankles.
Sitosterolemia can lead to heart disease, so a person might have symptoms such as chest pain or shortness of breath with exercise.

Diagnosis
Xanthomas and arthritis may be the first indications that a person has sitosterolemia. A special test can check the levels of cholesterol and plant sterols in the blood. Of sterols in the blood, cholesterol accounts for more than 99% and plant sterols about 0.2%. In sitosterolemia, cholesterol accounts for 80% and plant sterols about 20%. This high level of plant sterols in the blood would confirm the diagnosis.

Treatment
Once sitosterolemia is diagnosed, a diet low in plant sterols may be recommended. This would include:

  • Eliminate all sources of vegetable fats, including nuts, seeds, olives, and avocados
  • Eliminate vegetable oils, shortening, and margarine
  • Eliminate chocolate (high in plant sterols)
Since sitosterolemia can lead to heart disease, a cardiologist should be consulted. Arthritis may require treatment.

In October 2002 a cholesterol absorption inhibitor, the drug ezetimibe (Zetia), received U.S. Food and Drug Administration approval for use in sitosterolemia. The drug reduces the level of plant sterols in the blood. Drugs such as cholestyramine (Prevalite, Questran) which bind with bile acids in the digestive system achieve similar results.

Information for this article was taken from:
Steiner, R. D. (2004). Sitosterolemia. eMedicine, accessed at http://www.emedicine.com/ped/topic2110.htm

Explore Rare Diseases
By Category
About.com Special Features

8 Ways to Cut Drug Costs

Learn how to save money on medications with these recommendations. More >

Healthy Bodies, Healthy Minds

Keep yourself, and your family, happy and healthy this season. More >

We comply with the HONcode standard for trustworthy health information: verify here.
  1. Home
  2. Health
  3. Rare Diseases
  4. Rare Diseases A - Z
  5. Rare Diseases: S
  6. Sitosterolemia

©2009 About.com, a part of The New York Times Company.

All rights reserved.