ALS (amyotrophic lateral sclerosis, also called Lou Gehrig's disease), is a disease that attacks the nerve cells (motor neurons) that control muscles. Eventually, all the muscles that a person can ... Read More

The National Institutes of Health (NIH) has established the first integrated drug development program for treatments for rare diseases. Called the Therapeutics for Rare and Neglected Diseases program (TRND), it ... Read More

Narcolepsy is a nervous system disorder that causes excessive daytime sleepiness. People with narcolepsy involuntarily fall asleep, even while doing something like talking, eating, working, or while in school. These ... Read More

May 15 is International MPS Awareness Day. There is a group of genetic disorders called mucopolysaccharidoses (MPS) in which critical body enzymes (chemicals) are missing or not enough. Some of ... Read More

Idiopathic thrombocytopenic purpura (ITP), also called immune thrombocytopenic purpura, is a condition in which the body does not have enough platelets. ITP occurs in 50 to 150 people per million ... Read More

33 Variations, a play by Moisés Kaufman, has received 5 Tony Award nominations. Among them is Best Performance for a Leading Actress in a Play: Jane Fonda, for her portrayal ... Read More

Researchers at Yale University School of Medicine, New Haven, Connecticut, and their colleagues studied 403 adults with Gaucher disease Type 1 to see what their risk of cancer was compared ... Read More

Post-polio syndrome usually affects polio survivors 15 years or more after having had polio. Its main symptom is new muscle weakness or decreased endurance. Science fiction writer Arthur C. Clarke ... Read More