Genzyme Corp. and Dyax Corp. have announced a joint venture to continue the development of a drug to treat hereditary angioedema, a rare disease that causes attacks of subcutaneous, ... Read More

Since the early 1990s, research into cures for this group of inherited storage disorders has progressed. The genetic sources of Niemann-Pick have been identified, and successful treatment studies using ... Read More

Rapper Nelly and his sister, Jackie Donohue, have launched a campaign called "Jes Us 4 Jackie." The campaign held two bone marrow drives on June 21. Jackie has ... Read More

Genzyme Corporation is exploring using gene transfer therapy to replace the missing enzyme in Type A Niemann-Pick disease. This neurodegenerative disorder is caused by the almost complete lack of acid ... Read More